Mesenchymal stem/stromal cell (MSC)-based therapy holds promise for reversal of bone loss in osteoporosis. This phase 1 study establishes the safety and feasibility of intravenous administration of gl...

Latus Bio raised $42 million as it prepares to seek FDA approval to start a clinical trial for its gene therapy for Huntington's disease.

The study is now scaling up to do more in utero procedures and evaluate effects on disability as children grow

Pivotal Phase 3 randomized, double-blind, placebo-controlled study (n=106) met the primary endpoint (PUL v2.0) and the key secondary cardiac…...

Baby KJ's medical team intend to ask the FDA to start a clinical trial that would be open to patients with seven different urea cycle disorders.

Reimagining the future of healthcare through the power of gene therapy.

Sept 8, 2025, Bethesda, MD – The Association for the Advancement of Blood & Biotherapies (AABB) is pleased to announce the release of the first edition of Cell and Gene Therapy Standards for Pharmacy,...

/PRNewswire/ -- ScaleReady, in collaboration with Wilson Wolf Manufacturing, Bio-Techne Corporation (NASDAQ: TECH) and CellReady, today announced that eight...

Professor Aijun Wang won a $3.2 million NIH grant to develop a cure to Dup15q syndrome using an in-utero gene editing formula.

Reid et al. develop MultiVINE-seq to map thousands of non-coding disease variants to genes in human brain vascular cells. Cerebrovascular disease variants compromise vessel integrity, whereas Alzheime...

Lawmakers have snubbed health secretary RFK Jr. by including an amendment in a spending bill mandating that an agency under his purview continue to research messenger RNA vaccines.

Dr. Jerzy Kupiec-Weglinski has led organ transplant research at UCLA for nearly three decades. Kupiec-Weglinski, the vice chairman of basic science research in the David Geffen School of Medicine’s su...

Dr. Jerzy Kupiec-Weglinski has led organ transplant research at UCLA for nearly three decades. Kupiec-Weglinski, the vice chairman of basic science research in the David Geffen School of Medicine’s su...

The Government Accountability Office found that the Trump administration, by abruptly canceling NIH grants, had violated a 1974 federal law

An ex vivo organotypic and immunocompetent human leukaemia chip system is used for CAR T cell therapy modelling and screening of patient response.

After spearheading a 34% cut in cancer mortality, the National Cancer Institute at the NIH is bleeding resources and staff and could see its budget cut by nearly 40%.

A federal judge on Friday indefinitely blocked the Trump administration from revoking Harvard University��s ability to host international students and scholars while legal challenges continue.

Velazquez-Rivera et al. have developed and validated a set of new BEC-enhancer AAV vectors that allow for selective genetic labeling of, and access to, brain endothelial cells (BECs). These useful too...

This Week in Gene & Cell Therapy: Clinical Trial Expansions, Rare Disease Designations, and Breakthrough Manufacturing Approvals! 🧬 From Immix […] The post Cell and Gene Therapy Weekly News – May 29th 2025 appeared first on LucidQuest Ventures.

Our group is called  INDIVISIBLE Sacramento and we have a mission to defend democratic norms and institutions by sharing information with its members about current events and issues, promoting ci...

Productive science requires a great team, and that team develops together. That's one reason chaotic interference is dangerous for science.

Donald Trump won back the Oval Office and took charge of the government amid the strongest poll numbers of his political career, but as the 100-day mark of his presidency approaches, Americans’ views ...

At UC Berkeley, 12 students have had their status restored today after 23 were terminated since April 4.

The Women’s Health Initiative has produced numerous influential findings

STAT is tracking, day by day, what's happened in the words of science and health during the first months of the Trump administration.