Some comments on a proposed OMB research rule have been mysteriously removed from a public-facing government webpage.

Experts question technical improvements Huidagene tried when using a Duchenne muscular dystrophy treatment strategy largely abandoned by U.S. companies.

Prime Medicine said it had won an arbitration dispute against Beam Therapeutics, a clash that had pitted two well-backed gene-editing companies against each other.

Bluebird Bio was a dark biotech morality tale when David Meek bought it. He says the new company, Genetix, is already making money.

The lawmaker spent nearly two decades voting against paid leave.

In a Q&A, Kenneth Chien, no longer with Moderna, predicts the company's mRNA cancer vaccine will be transformative for biotech.

In a Q&A, Kenneth Chien, no longer with Moderna, predicts the company's mRNA cancer vaccine will be transformative for biotech.

The use of genome editing in early embryos has pulled back the curtain on the role of one of the key genes that orchestrates the first stages of human development, researchers reported.

Exclusive: STAT has learned that Eli Lilly and the FDA allowed a 79-year-old to gain extraordinary access to an experimental obesity drug through the agency’s “compassionate use” program.

A demonstrator who shot and wounded a police officer during a protest outside a Texas immigration center July 4 has been sentenced to 100 years in federal prison.

Strategic divestment of consumer media portfolio enables Springer Nature to focus on its core business Transaction supports the long-term development

A new memo from the Department of Justice seeks to upend landmark disability laws and court rulings.

“As a physician and former public health official, I have never been more concerned about those rates of congenital syphilis,” writes Jeffrey D. Klausner.

Congenital syphilis should be preventable. An Arizona case shows how drug shortages and procedural hurdles are fueling a growing public health crisis.

Medicaid cuts and fraud crackdown trickle down to states, threatening people with disabilities.

Alcohol kills more Americans each year than all other drugs combined. Why does the U.S. ignore its most harmful substance use crisis? Alcohol kills more

Some boys had astonishing recoveries. But other boys died. Now Astellas is returning to revised gene therapy for XLMTM.

State restrictions, Trump administration policies, and waning public support are further limiting adults' access to transgender care

Daraxonrasib, a pancreatic cancer drug from Revolution Medicines, is showing unprecedented success. For patients like Leanna Stokes, survival time doubled.

In a trial, metastatic pancreatic cancer patients on the medicine lived twice as long as those on chemotherapy.

CAR-T therapy is toting up more remissions in autoimmune disease, and generating a flood of experimentation and investment.

A mother's persistence helps revive an all-but-abandoned drug class and could aid her son and thousands of others with neuromuscular conditions.

Over the last year, through fear and intimidation, the Trump administration has succeeded in shrinking transgender adolescents’ access to gender-affirming care. One by one, programs that previously se...

Stanley Plotkin, the 93-year-old "godfather of vaccines," is watching his field’s achievements slip away.

Thirty years after scientists demonstrated how brain implants can help rhesus monkeys move robotic limbs using only their mind, the clinical pathway for the technology is still a little out of focus.

Lobbyists told STAT they believe the odds of approval go up if a decision can be spun as a win for the Trump administration.

STAT has won its fourth Polk Award in five years for documenting the Trump administration’s shakeup of the FDA, scientific research, and public health.

The FDA reversed course and told Moderna it would review its application for a new flu vaccine, the company announced Wednesday.

Vertex is running out of time to establish Casgevy as a transformative treatment for sickle cell.

Why Bristol Myers Squibb is banking on a decades-old drug to help secure its future.

FDA paused trials for two experimental gene therapies from Regenxbio after one child developed a brain tumor.

A new FDA pathway meant to enable one-time gene-editing cures could, ethicists warn, become a Pandora's box.

At least a dozen biotech companies are developing tools to diagnose endometriosis more easily.

A new FDA pathway meant to enable one-time gene-editing cures could, ethicists warn, become a Pandora's box.

The number of recommended childhood shots drops from 17 to 11.

An eight-decade partnership between universities and the federal government made U.S. science preeminent. It took Trump less than a year to shred that

3 key issues to watch at FDA as Makary struggles to stabilize the agency

Lung transplant patient Hannah Goetz’s life depended on the generic version of the critical drug tacrolimus. It was supposed to be equivalent to the brand-name medication — but the FDA doesn’t always ...

CDC awards grant to controversial Danish researchers with ties to top FDA official Tracy Beth Høeg.

The Trump administration intends to make its most forceful attempt yet at restricting gender-affirming care for transgender youth in the U.S.