US officials are working with a small biotech company to provide an experimental treatment that may be used in patients exposed to Ebola, according to a person familiar with the matter.

Big Pharma is pouring money into tech-devised treatments, but the verdict is out on whether they’ll actually work.

Virologist María Inés Barría remembers the Eureka moment from a decade ago.

Marty Makary’s exit as head of the Food and Drug Administration is giving the biotech industry hope for stability after months of turmoil.

Analysts cut Cobenfy expectations as patients struggle to get the new drug.

Biogen Inc. has agreed to acquire Apellis Pharmaceuticals Inc. for $5.6 billion, expanding its treatments in immunology and rare diseases in one of the company’s largest-ever acquisitions.

The revolving door at the Food and Drug Administration has pushed out another top official: Vinay Prasad, the controversial head of the agency’s vaccine and gene therapy arm, will depart in April.

A key US Republican senator said he’s launched an investigation into the Food and Drug Administration’s recent denials of treatments for rare diseases, adding political pressure on an agency that’s al...

The head of the US Food and Drug Administration’s division of vaccines and gene therapies is leaving the agency after a tumultuous tenure, sending biotech shares higher in late trading on Friday.

Katie Jackson desperately wants a new treatment for Huntington’s disease. Her husband died from the devastating brain disorder. And because the disease runs in families, her three children have a 50% ...

Moderna Inc.’s chairman says the Trump administration’s vaccine policy changes are part of a broader attack on science that may have only just begun.

Leading to overcharges, treatments that don’t extend lives and failed implants.

Pharma companies are spending billions on a treatment based off old drugs, with little evidence it will extend lives.

Hi, it's Gerry in New York, where schools have banned smartphones in the classroom for the first time. I spoke to one high school student in a neighboring state about how a phone ban at his school has...

A top US regulator plans to unveil a faster approach to approving custom gene-editing treatments, a move designed to unleash a wave of industry investment that will yield cures for patients with rare ...

Exclusive: The inside story of why Moderna now faces a crisis unlike any in its 15-year-history.

Some experts worry that patient groups’ growing influence is leading to the approval of drugs that may not work and could sometimes be dangerous.

Hi, it’s Gerry in New York. Researchers are trying to build on the success of “baby KJ” and make more personalized treatments for kids with rare diseases. More on that in a moment, but first ...

US regulators approved Moderna Inc.’s Covid vaccine for children, but for a narrower group than before, continuing Robert F. Kennedy Jr.’s controversial policy that restricts access to the shots for s...

US cases are the highest they’ve been since the virus was declared eradicated 25 years ago. The health secretary’s anti-vax agenda is part of the reason.

Pediatricians weigh the risks of vaccinating ahead of schedule with threat of shot shortages looming.

The Department of Health and Human Services is retiring the 17 members of a committee of government vaccine advisers, Secretary Robert F. Kennedy Jr. said Monday.

US Health and Human Services Secretary Robert F. Kennedy Jr. said the Covid shot has been taken off of the country’s recommended vaccine list for healthy children and pregnant women, a seismic shift i...

High-margin inoculations bring more customers into drugstores.

US regulators will no longer approve booster shots to prevent Covid infections for healthy adults and children without new clinical trials showing they are still safe and effective, adding a costly ne...

Senior leaders at the US Food and Drug Administration began pushing Moderna Inc. and Pfizer Inc. to file for full, formal approval of their Covid vaccines for children last summer. The conversations g...

Despite the known risks of patients experiencing life-threatening side effects, prescribing standards vary widely among medical centers.

Vertex Pharmaceuticals Inc.’s new non-opioid painkiller is being placed on a tier that means it might be costlier than other pain treatments on UnitedHealth Group Inc.’s approved drug lists.

A gene therapy from Regeneron Pharmaceuticals Inc. improved hearing in nearly all deaf children in a clinical trial, results that could allow the company to seek regulatory approval for the one-time t...

Firing thousands of employees at the agencies that oversee our food supply, research cures for cancer and monitor disease outbreaks is shortsighted.

President Donald Trump’s end of diversity, equity and inclusion language in federal agencies has caused US health data to be removed or not be updated. Medical experts say the extensive losses, even i...

Hi, it’s Damian in New York, where I watched the RFK Jr. Q&A and wondered whether anyone had ever uttered “amyloid” in a senate hearing before. More on that hearing in a moment, but first ...

Vertex Pharmaceuticals Inc. gained US approval for the first new type of painkiller in more than two decades, paving the way for a safer alternative to addictive opioids that have been linked to hundr...

US officials are investigating the appearance of a strain of bird flu identified in the US for the first time, a worrying sign that the virus is evolving in ways that could make it harder to contain.

Robert F. Kennedy Jr. earned millions from his work as an attorney, including referral fees from cases filed against the agency he’s been chosen to lead, federal disclosures show.

Greetings from Michelle in snowy Washington, DC, where I’m grappling with flashbacks. It was 18 degrees and snowing in Minnesota when I dove into Lake Minnetonka on New Year’s Day. Insanity? Perhaps. ...

Vertex Pharmaceuticals Inc.’s nonaddictive drug for lower back pain didn’t do better than a placebo in a midstage trial, causing the company’s shares to fall.

At a time when geopolitical tensions are hitting industries from semiconductors to electric vehicles, pharmaceutical dealmaking has become a rare bright spot for collaboration between China and the We...

Donald Trump has picked a raft of medical contrarians and government outsiders to run the nation’s top health agencies, alarming experts who are bracing for changes to vaccines and other bedrock treat...

Surgeon and author Marty Makary is seen as the leading candidate to run the US Food and Drug Administration under President-elect Donald Trump, people familiar with the matter said.

His promotion of bizarre conspiracy theories could turn the government into an “accelerant for misinformation.”