Reposted by AZLatina
Regenxbio says gene therapy strengthened boys with Duchenne muscular dystrophy; muscle performance tests in small trial seen as step to accelerated approval
www.statnews.com/2024/11/18/d...
statnews.com
Regenxbio says gene therapy strengthened boys with Duchenne muscular dystrophy
Based on a small trial with positive muscle performance data, Regenxbio is expected to pursue approval of its gene therapy for Duchenne muscular dystrophy.
