Congratulations to the whole team @regeneron.com!It is incredibly rewarding to see basic research translate into something so meaningful for patients. This is what science can achieve with patience, persistence, and a long-term vision #FOP investor.regeneron.com/news-release...
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Pasatru™ (garetosmab-grts) First and Only FDA-approved Treatment Demonstrating Reduction in New Heterotopic Ossification (HO) Lesions and Clinician-Assessed Flare-ups in a Placebo-controlled Trial in ...
FOP is an ultra-rare genetic disorder characterized by rogue bone formation that infiltrates muscles, tendons, ligaments and other connective tissues, resulting in significant disability Approval bas...