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American Society of Gene + Cell Therapy

@asgct.bsky.social
1K followers 36 following 250 posts

Advancing knowledge, awareness, and education leading to the discovery and clinical application of genetic and cellular therapies to alleviate human disease.

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American Society of Gene + Cell Therapy @asgct.bsky.social · 29/09/2026
On-demand access to our 2026 Policy Summit is now available! Catch up on the conversations you missed or rewatch your favorite sessions. Access on-demand now ➡️ www.asgct.org/events-meetings/2026-…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 24/09/2026
ASGCT and NTSAD are launching the inaugural NTSAD-ASGCT Translational Research Fellowship Program to help advance innovative genetic medicine research for rare neurogenetic diseases. Learn more about the fellowship, eligibility criteria and application deadlines: bit.ly/4hciETk
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American Society of Gene + Cell Therapy @asgct.bsky.social · 23/09/2026
Join the 2026 NORD Breakthrough Summit, Oct. 25–27 in Washington, D.C.! ASGCT staff will be there to connect you with patient education resources and discuss the latest policies affecting rare disease research and individuals. Learn more ➡️ nordsummit.org #NORDSummit #RareDisease
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American Society of Gene + Cell Therapy @asgct.bsky.social · 22/09/2026
🔬 Don't wait for the Annual Meeting to share your latest science! Submit your late-breaking abstract for Breakthroughs in Cell + Gene Therapy by Monday, October 12, 2026. Learn more and submit now ➡️ bit.ly/4wHH10l
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American Society of Gene + Cell Therapy @asgct.bsky.social · 14/09/2026
Submit an abstract to the Inaugural Canadian Gene and Cell Therapy Conference by October 1! For more information or to submit an abstract, visit cancgt.ca.
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American Society of Gene + Cell Therapy @asgct.bsky.social · 08/09/2026
📢 We're less than one week away from the 2026 Policy Summit! Register now ➡️ bit.ly/4wIMIem #ASGCTadvocacy #PS26
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American Society of Gene + Cell Therapy @asgct.bsky.social · 26/08/2026
The FDA has approved Genglycos, an AAV gene therapy developed by Ultragenyx Pharmaceuticals. Read our full blog post about the approval here: bit.ly/3SbpDlN
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FDA Approves Genglycos, First Gene Therapy for GSDIa
The unbiased source for reliable, scientific information, news, and breakthroughs in gene and cell therapy.
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American Society of Gene + Cell Therapy @asgct.bsky.social · 25/08/2026
📰 Our latest edition of The Patient Press newsletter is now available! This month, read updates about OMB, check out our two new Patient Education resources, catch up on our recent Congressional Briefing on CGT for Rare Disease, and more. Read The Patient Press now ➡️ bit.ly/4il1BiC
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American Society of Gene + Cell Therapy @asgct.bsky.social · 30/07/2026
🎙️ Meet Anna Maurer, PhD in our newest episode of Scientists, Unedited. Recorded live at the 2026 Annual Meeting in Boston, host Eirini Vamva, PhD talks with Dr. Maurer about growing up in Michigan, studying at Harvard Medical School, and her work in AAV. Listen now! ➡️ bit.ly/44O6hpt
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American Society of Gene + Cell Therapy @asgct.bsky.social · 28/07/2026
Hear from leading minds in oncology at this fully virtual event! Join us Oct 14-15 to learn about the innovative approaches reshaping cancer treatment while addressing the critical challenges currently facing the field. Register now ➡️ bit.ly/4aX9OVW
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American Society of Gene + Cell Therapy @asgct.bsky.social · 24/07/2026
From blood cancers to autoimmune diseases, CAR T-cell therapy is expanding far beyond its original boundaries. Start learning in our latest content collection: learning.asgct.org/courses/238146
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American Society of Gene + Cell Therapy @asgct.bsky.social · 20/07/2026
A new stage for Breakthroughs: Join us in Nashville! Customize your experience across three concurrent tracks covering translation & manufacturing, biological precision, and the new therapeutic architectures overcoming challenges in the central nervous system: asgct.org/breakthroughs
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American Society of Gene + Cell Therapy @asgct.bsky.social · 15/07/2026
ASGCT's advocacy on OMB's proposed Uniform Guidance reforms continues. This month, the Society submitted comments urging OMB to withdraw the rule, led a coalition letter to Congress, and launched grassroots outreach to protect #CGT research. Read more: bit.ly/4voQvvR #ASGCTAdvocacy
asgct.org
The Advocate: July 2026
ASGCT's advocacy on OMB's proposed Uniform Guidance reforms continues. This month, the Society submitted comments urging OMB to withdraw the rule, led a…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 14/07/2026
Fyodor Urnov, 2026 ASGCT Catalyst Award co-recipient, joins this episode of The Issue to discuss the rapid evolution of gene-editing technology and the critical role of industry-wide collaboration in bringing life-changing therapies to patients. 🎧 Listen: bit.ly/4h8nDob
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American Society of Gene + Cell Therapy @asgct.bsky.social · 10/07/2026
How is innovation advancing cell and gene therapy manufacturing? Read our #ASGCT2026 recap on how automation, analytics, and regulatory readiness are shaping the future of CGT development: bit.ly/4aXWNLV
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Advancing CGT Manufacturing and Regulation Through Innovation and…
At ASGCT’s 2026 Annual Meeting, leaders from the FDA, industry, and academia came together to discuss technologies and regulatory approaches shaping the…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 09/07/2026
Level up your cell and gene therapy experience in just one day! Dive into real-world applications of AAV, CAR T, and HSC modalities, clinical management of toxicities, and the future of individualized medicine at this focused, one-day event at @nationwidekids.bsky.social! Details: asgct.org/gme
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American Society of Gene + Cell Therapy @asgct.bsky.social · 08/07/2026
Looking for a community that supports your career and keeps you connected to the latest in the field? Join ASGCT this summer and save up to 15% on your dues! asgct.org/become-a-member
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American Society of Gene + Cell Therapy @asgct.bsky.social · 07/07/2026
These $100K awards provide vital financial and professional development support to postdoctoral or early-career members from groups that have historically faced limited access to research opportunities, mentorship, or career advancement resources in science. asgct.org/expanding
asgct.org
Expanding Pathways Fellowship
These awards are designed for postdoctoral or early-career members from groups that have historically faced limited access to career advancement in…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 07/07/2026
FDA approved Tregzi, an allogeneic cell therapy using Tregs to reduce complications of allo-HSCTs. This approval is an important advancement for patients with blood cancers. ASGCT President Dr. Matt Porteus shares what this approval means for the #CGT field: bit.ly/44RGgW0
asgct.org
FDA Approves Allogenic Immunotherapy for Blood Cancers with Reduced...
This approval represents an important advancement for patients with blood cancers, demonstrating the potential to improve the safety and effectiveness of...
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American Society of Gene + Cell Therapy @asgct.bsky.social · 06/07/2026
The ASGCT Policy Summit is uniquely designed to break down silos and spark real collaboration with the stakeholders driving the future of cell and gene therapy policy. Join us September 14 in Washington, D.C., or online: asgct.org/policysummit
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American Society of Gene + Cell Therapy @asgct.bsky.social · 02/07/2026
Recorded live at #ASGCT2026, listen as Molecular Therapy Advances Editor-in-Chief Dr. Mohamed Abou-el-Enein sits down with Drs. Jennifer Adair, Claire Booth, Terence Flotte, and Donald Kohn to discuss the evolving landscape of rare disease therapies: bit.ly/4v6eHDj
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American Society of Gene + Cell Therapy @asgct.bsky.social · 01/07/2026
Applications are open for the ASGCT Career Development Awards, offering vital financial support to early-career scientists and postdocs driving innovation in the field. Don't miss the chance to fund your research and grow your network. Apply today: asgct.org/cda
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American Society of Gene + Cell Therapy @asgct.bsky.social · 30/06/2026
The latest Patient Press is here! Catch up on crucial updates on proposed federal grant changes, our brand-new cell and gene therapy coloring book, a new Community Quick Take, and the latest clinical trial breakthroughs in rare disease research. bit.ly/4gdItSK
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The Patient Press: June 2026
We're breaking down how the OMB Proposed Rule affects medical research and future treatments. Plus, check out our new coloring book and the latest patient…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 30/06/2026
Biomedical innovation depends on stable research funding. We're leading a sign-on letter opposing proposed OMB changes that could slow progress in #CGTs. Organizations can sign by July 15 at 12 p.m. ET. 🔗 Sign here: bit.ly/4gdQ8AA
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American Society of Gene + Cell Therapy @asgct.bsky.social · 29/06/2026
FDA approval is only the first step in bringing cell and gene therapies to patients. At #ASGCT2026, experts explored the challenges that continue to limit patient access and how value-based payment models and cross-sector collaboration can help build more sustainable pathways. bit.ly/4yciBNR
asgct.org
Building Sustainable Access Pathways for Cell and Gene Therapies
As more cell and gene therapies (CGTs) move from development into clinical practice, stakeholders across the healthcare system are increasingly…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 26/06/2026
As we kick off our 2027 awards cycle, we invite you to take a moment to nominate your colleagues, mentors, mentees, and fellow collaborators for an ASGCT Honorific Award! bit.ly/4aE0A0L
asgct.org
Behind Every Award is a Nomination: ASGCT is Now Accepting…
As we kick off our 2027 awards cycle, we invite you to take a moment to nominate your colleagues, mentors, mentees, and fellow collaborators for an ASGCT…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 25/06/2026
What does the path to leadership in cell and gene therapy look like? Scientists, Unedited host Eirini Vamva, PhD, sits down with ASGCT President Matthew Porteus, PhD, for a candid conversation about his journey, motivations, and life beyond the lab. 🎧 Listen: bit.ly/4uZYFea
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American Society of Gene + Cell Therapy @asgct.bsky.social · 24/06/2026
In rare disease research, traditional clinical trials aren't always possible. Check out this Community Quick Take to learn how patient data is helping researchers go beyond the placebo control and accelerate life-changing treatments. ▶️ Watch now: bit.ly/4fLiguF
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American Society of Gene + Cell Therapy @asgct.bsky.social · 24/06/2026
📢 Registration and abstract submissions are officially open for Breakthroughs in Cell & Gene Therapy! Explore our 2026 program tracks, view abstract categories, and secure your spot today: asgct.org/breakthroughs
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American Society of Gene + Cell Therapy @asgct.bsky.social · 23/06/2026
From dreaming about genetics since high school in Nigeria to tackling the field's biggest immune challenges as a University of Missouri PhD candidate, Godwin Iroanya's journey is all about making the "impossible" possible. Listen now: bit.ly/4ewfqaB
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American Society of Gene + Cell Therapy @asgct.bsky.social · 19/06/2026
#WorldSickleCellDay reminds us of the critical importance of advancing awareness, fostering connection, and driving equitable progress for every individual and family impacted by SCD. ❤️ Hear from sickle cell warriors in this session from the 2026 Empowering Patients Summit: bit.ly/4os6ojo
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American Society of Gene + Cell Therapy @asgct.bsky.social · 19/06/2026
How are patient-centered approaches shaping the future of cell and gene therapy development? Check out the key takeaways from our recent Annual Meeting symposia on aligning patient experience, regulatory strategy, and clinical trial design. Read the full recap: bit.ly/4vKIt18
asgct.org
Patient-Centered Innovation in Rare Disease CGTs at ASGCT 2026 Annual…
Across both symposia, a consistent message emerged: advancing cell and gene therapies for rare diseases requires continued evolution in how patients are…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 18/06/2026
Bringing a cell or gene therapy from concept to patient requires more than great science. The 2026 ASGCT Policy Summit dives into the full arc of CGT development, from pipeline funding and regulatory strategy through manufacturing, payment policy, and patient access. Join us:: asgct.org/policysummit
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American Society of Gene + Cell Therapy @asgct.bsky.social · 18/06/2026
Get to know the new co-hosts, Jason West, PhD, and Sanjay D’Souza, PhD, as they share their backgrounds, ask each other questions, and share how listeners can get involved with future content of The Issue podcast. 🎧 Listen now: bit.ly/4vUjSXA
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American Society of Gene + Cell Therapy @asgct.bsky.social · 17/06/2026
OMB has proposed significant changes to the federal grantmaking framework, including provisions affecting peer review, international collaboration, and scientific communication. Read more in the latest Advocate: bit.ly/4vzU1op #ResearchFunding #CGT #ASGCTAdvocacy
asgct.org
The Advocate: June 2026
OMB has proposed significant changes to the federal grantmaking framework, including provisions affecting peer review, international collaboration, and…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 17/06/2026
While AAV and LNPs continue to revolutionize the field, translating these powerful delivery platforms into safe, predictable, and scalable clinical therapies presents unique challenges. We're partnering with @childrensphila.bsky.social for this comprehensive, one-day event: bit.ly/4uK4PPz
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American Society of Gene + Cell Therapy @asgct.bsky.social · 16/06/2026
How has ASGCT membership shaped a career in regulatory policy? Hear from Dylan Bechtle, Director of Regulatory Policy at Johnson & Johnson, on how the ASGCT community and resources have been invaluable for navigating the fast-moving cell and gene therapy space. 🎧 Listen now: bit.ly/3Q0zvxG
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American Society of Gene + Cell Therapy @asgct.bsky.social · 11/06/2026
It's never been easier to start building your foundational knowledge of CGT! Our Foundations of Cell & Gene Therapy online course is: ✔️ 100% free ✔️ Entirely self-paced ✔️ Led by field experts Choose a module and start learning today: bit.ly/4tmnsIK
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American Society of Gene + Cell Therapy @asgct.bsky.social · 04/06/2026
Proposed federal grant rule changes could affect how CGT research is reviewed, funded, and managed – including new limits on conference attendance, publication expenses, and international collaborations. Learn what's proposed and how to weigh in: bit.ly/4vusiou #ASGCTAdvocacy
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Proposed Changes to Federal Grant Rules – Significant Implications…
On May 28, 2026, the U.S. Office of Management and Budget (OMB) published a proposed rule that would significantly revise the Uniform Guidance – the…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 04/06/2026
Designed specifically for the next generation of medical leaders, this focused, one-day program provides the critical insights needed to navigate the rapidly evolving clinical landscape of cell and gene therapies. Learn more and register: asgct.org/gme
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American Society of Gene + Cell Therapy @asgct.bsky.social · 03/06/2026
Our premier policy event is returning to Washington, D.C.! Join us on September 14 to connect directly with key decision-makers, advocate for the field, and drive the critical conversations shaping the future of cell and gene therapy. Secure your spot today: asgct.org/policysummit
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American Society of Gene + Cell Therapy @asgct.bsky.social · 02/06/2026
New ASGCT member Dr. Mark Deehan (Mass General Hospital) discusses how his ASGCT Career Development Award, funded by the Foundation for Angelman Syndrome Therapeutics, is fueling new progress in his lab's research. 🎧 Listen now: bit.ly/4nXDck9
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American Society of Gene + Cell Therapy @asgct.bsky.social · 02/06/2026
Ready to take your research to the next level? Early-career researchers and emerging investigators are invited to apply for these $100K grant opportunities: ✔️ Career Development Award: asgct.org/cda ✔️ Expanding Pathways Fellowship: asgct.org/expanding
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American Society of Gene + Cell Therapy @asgct.bsky.social · 26/05/2026
Patient advocate Chrissy Green (Finding Hope for Frizzle) joins host Ben McLeod to discuss her parent-led organization's mission to develop an FRRS1L treatment and how the ASGCT Annual Meeting helps bridge the gap between advocacy and scientific development. 🎧 Listen now: bit.ly/43t3zF1
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American Society of Gene + Cell Therapy @asgct.bsky.social · 21/05/2026
Can RNA therapeutics close the gap for the 10% of cystic fibrosis patients without an approved treatment? Dr. Paloma Giangrande (MTNA) and Normand Allaire (Cystic Fibrosis Foundation) discuss an innovative new ASO-based approach in our latest episode. 🎧 Listen now: bit.ly/4uwBRDu
asgct.org
A CFTR mRNA isoform for the treatment of 3’ CFTR PTC variants… | ASGCT
Dr. Paloma Giangrande (Molecular Therapy Nucleic Acids) joins Normand Allaire (Cystic Fibrosis Foundation) to discuss an innovative ASO-based approach…
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American Society of Gene + Cell Therapy @asgct.bsky.social · 21/05/2026
ASGCT submitted written testimony to three FY27 appropriations subcommittees urging robust funding for NIH, ARPA-H, and CBER – and led a sign-on letter from 100+ organizations in support. Read more in the Advocate: www.asgct.org/advocacy/the-advocate…
asgct.org
The Advocate: May 2026
ASGCT tells Congress to Support Robust Funding for FDA, and Research Agencies
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American Society of Gene + Cell Therapy @asgct.bsky.social · 20/05/2026
Divergent regulatory expectations remain a major hurdle for cell and gene therapy developers and patient access worldwide. Join us for a free webinar on June 24 to hear from the ICH Cell & Gene Therapy Discussion Group: bit.ly/3RBl2s4
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American Society of Gene + Cell Therapy @asgct.bsky.social · 20/05/2026
#ASGCT2026 brought together thousands of clinicians, scientists, industry leaders, and patient advocates for an incredible week of groundbreaking science and connection. Mark your calendars – we can't wait to see you all in Philadelphia for #ASGCT2027, May 3–7, 2027!
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American Society of Gene + Cell Therapy @asgct.bsky.social · 19/05/2026
Recorded live at #ASGCT2026, host Ben McLeod catches up with Dr. Marco Carpenter of @childrensphila.bsky.social. Dr. Carpenter discusses his research journey, the evolving landscape of cell and gene therapy, and how the ASGCT community supports early-career researchers: bit.ly/4uXJn9V
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American Society of Gene + Cell Therapy @asgct.bsky.social · 19/05/2026
The ASGCT office has a new home! Find us at 20700 Swenson Drive, Suite 200 in Waukesha, Wisconsin.
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