Lilly to acquire Verve Therapeutics to advance one-time treatments for people with high cardiovascular risk

CRISPR Stocks in Wake of Verve Therapeutics Acquisition by Eli Lilly

NTLA-2002 More and More Looks Like a Cure for HAE

uniQure Announces Appointment of Kylie O’Keefe as Chief Customer and Strategy Officer

MAHA Vows to Disrupt Sick-Care Model in Favor of Cures

2nd Patient with Chronic Granulomatous Disease Successfully Treated with Prime Editing

Grade 4 Liver Enzyme Elevation in Intellia’s Phase 3 ATTR Amyloidosis Trial

Grade 4 Liver Enzyme Elevation in Intellia’s Phase 3 ATTR Amyloidosis Trial

Dr. Martin Makary on X: "The physician patient relationship is sacred and when the government tries to become your doctor, we don’t have a great track record. Our job at the FDA is to review data and decide whether products are safe and effective. The FDA is not your doctor. https://t.co/odWpWU7ngh" / X

U.S. FDA Grants Platform Technology Designation to the Viral Vector Used in SRP-9003, Sarepta’s Investigational Gene Therapy for the Treatment of Limb Girdle Muscular Dystrophy Type 2E/R4

Bestuur biotechbedrijf Proqr doorstaat aanval Van Herk

New CBER chief Prasad promises to 'rapidly' push even small advances for rare disease drugs

CBER Roundtable on Cell and Gene Therapy

RNAi Therapeutics A Bright Spot In Dark Biotech Winter

uniQure Provides Regulatory Update on AMT-130 for Huntington’s Disease | uniqure BV

BioNTech and Bristol Myers Squibb Announce Global Strategic Partnership to Co-Develop and Co-Commercialize Next-generation Bispecific Antibody Candidate BNT327 Broadly for Multiple Solid Tumor Types

Protagonist and Takeda Announce ASCO Plenary Presentation Highlighting Full 32-Week Results from Phase 3 VERIFY Study of Rusfertide, Showing Reductions in Phlebotomy, Improved Hematocrit Control in Po...

Modeling Reemergence of Vaccine-Eliminated Infectious Diseases Under Declining Vaccination in the US