nature.com
First for RNA therapy: man with rare motor-neuron disease, also called ALS, improves after treatment and continued to work as a physician a year after becoming the first person to receive a drug designed to target the specific genetic mutation that…
First for RNA therapy: man with rare motor-neuron disease, also called ALS, improves after treatment and continued to work as a physician a year after becoming the first person to receive a drug designed to target the specific genetic mutation that causes his disease.