"It’s actually a good thing we have to worry about our kids dying from this product, because it means we have a product to be worried about," he said. "If you don’t do anything for a young man with Duchenne, he’s going to die."
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Two boys died after a gene therapy. This family won’t give up hope.
The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients died, the drug’s manufacturer halted dosing under pressure from the FDA.
