Our colleagues Caroline Mussert and Frank Leebeek, together with the @isth.org SSC working group on gene therapy, have developed Metro Maps care pathways for Hemophilia A and Hemophilia B gene therapy. www.jthjournal.org/article/S153...
jthjournal.org
A comprehensive care pathway of gene therapy for hemophilia based on current guideline documents and Summary of Product Characteristics (SMPCs); Communication from the ISTH SSC Working Group on Gene T...
Gene therapy for hemophilia has recently been implemented as standard clinical care,
requiring organizational and multi-stakeholder preparedness and clear guidelines.
In addition to pharmaceutical Sum...
